Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated commercial-stage biotechnology company advancing genetic medicines for rare and life-threatening diseases, focused on inherited cardiovascular disorders,
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated commercial-stage biotechnology company advancing genetic medicines for rare and life-threatening diseases, highlighted key findings and development
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, commercial-stage biotechnology company advancing genetic medicines for rare and life-threatening diseases, focused on inherited cardiovascular disorders,
FDA confirms pivotal efficacy population of 12 patients, including the first three treated under the modified protocol
FDA review of initial safety data supports continued enrollment and dosing under modified
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, commercial-stage biotechnology company advancing genetic medicines for rare and devastating diseases, focused on inherited cardiovascular disorders, today
All three initial patients treated with RP-A501 under the modified pivotal Phase 2 protocol completed the protocol-defined safety observation period; no thrombotic microangiopathy, capillary leak syndrome, or other
Initial three patients were treated safely; RP-A501 was well-tolerated with no TMA or capillary leak syndrome observed
Rocket is actively engaging with the FDA to align on the path to pivotal trial completion;
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, commercial-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today announced the
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, commercial-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today announced that
Pivotal Phase 2 trial of RP-A501 for Danon disease progressing with dosing reinitiated
First patient dosing in Phase 1 study of RP-A701 for BAG3-related dilated cardiomyopathy anticipated in
PRV monetization provides $180 million in non-dilutive capital to support cardiovascular pipeline
Cash runway extended into the second quarter of 2028
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated,
First FDA-approved gene therapy for children with severe LAD-I due to biallelic variants in ITGB2
Severe LAD-I is an ultra-rare, life-threatening pediatric genetic immunodeficiency characterized by recurrent
Pivotal Phase 2 trial of RP-A501 for Danon disease to resume in 1H 2026
KRESLADI™ for severe LAD-I on track for March 28, 2026 PDUFA date
Dosing of first patient in Phase 1 study of RP-A701 for BAG3-related
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today announced that the
Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today announced that the